Unlock Hope: Download Our Pediatric Gene Therapy Case Study
Learn about the amazing collaboration between Veristat and a mid-size biotech company that led to the development of a revolutionary gene therapy program for an extremely rare pediatric neurological condition. Our case study highlights the launch of a Phase I/II clinical trial following a successful natural history study, the obstacles that were overcome through global coordination, and the full-service support provided by Veristat as the sponsor's implementation arm, ensuring the best possible experience for patients. Join us in making a significant impact on pediatric healthcare by downloading the case study today.
Download our case study to be part of the journey towards pediatric healthcare innovation and hope.
Download the Case Study
Bringing End-to-End Support in Clinical Trials for Biologics
We understand how high the stakes are for your biotherapeutic. Nothing is standard in developing biologic therapies, demanding more complex clinical program planning, and involving a complicated regulatory approval process.
As your strategic partner, Veristat ensures that your clinical trial or program design supports your regulatory strategy in this specialized area. Our experienced teams are ready to plan and launch your biologics trial:
- Full-service clinical trial planning and project management
- Clinical site management and monitoring
- Biometrics expertise including data management, biostatistics, statistical programming, and data standards implementation
- Medical writing of clinical trial and regulatory submission documentation
- Strategic regulatory consulting including tailored CMC support
- Preparation of regulatory marketing applications
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